What is Zolgensma used for?

( ARTG ) ZOLGENSMA (onasemnogene abeparvovec) is indicated for the treatment of paediatric patients with 5q spinal muscular atrophy (SMA) with bi-allelic mutations in the survival motor neuron 1 (SMN1) gene with 3 or fewer copies of the SMN2 gene. (Refer to Dosage and Method of Administration, section 4.2, Special Populations, paediatric patients and section 5.1 Clinical Trials).

What are the side effects of Zolgensma?

This medicine is under additional monitoring as it is new or being used in a different way. You can help identify new safety information by reporting any side effects you may get. You can report side effects to your doctor, or directly at www.tga.gov.au/reporting-problems . For more information on the Black Triangle Scheme and how to report side effects, see www.tga.gov.au/black-triangle-scheme

Can Zolgensma be used during pregnancy?

( AHT ) For the active ingredient onasemnogene abeparvovec You should seek advice from your doctor or pharmacist about taking this medicine. They can help you balance the risks and the benefits of this medicine during pregnancy.

OTC

Zolgensma

Kit

Data updated: 2026-05-02

Available in:

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KIT

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About This Product

Manufacturer

Novartis Gene Therapies, Inc.

Source

User Reviews

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